Jesy Nelson gave birth to her twin girls prematurely in May 2025 - now she's revealed her six-month-olds have been diagnosed ...

Researchers have identified a protein that’s critical to the development of skeletal muscle mass and strength and the tissue’s ability to metabolize glucose. They say their findings may lead to ...

Emma Ciafaloni, MD, FAAN, explores the groundbreaking approval of onasemnogene abeparvovec-xioi for spinal muscular atrophy and its impact on the treatment paradigm for this rare disease. This is a ...

Jesy Nelson details the months of hospital visits, unanswered worries, and the race for treatment after learning both of her ...

Former Little Mix star breaks down as she explains eight-month-old Ocean and Story have severe SMA and may never walk ...

A new clinical trial has revealed encouraging results for a muscle-targeting therapy aimed at improving motor function in children and adolescents with spinal muscular atrophy, according to a study ...

The first prenatal treatment for spinal muscular atrophy showed promise in a single case report. Risdiplam was given to the mother during pregnancy and to the child after birth. More than 2 years ...

Please provide your email address to receive an email when new articles are posted on . The study examined 26 newborns with spinal muscular atrophy given Evrysdi. Data showed 81% of babies were able ...

British pop star Jesy Nelson has made a heartbreaking admission about her twin baby daughters revealing they will “probably ...

Jesy Nelson has bravely shared that her twin daughters have been diagnosed with an incurable muscle disease (SMA type 1) and ...